Cancer ( Various Types)
Systemic Lupus Erythematosus (SLE)
Osteoporosis Paget's Disease of Bone
Urea Cycle Disorders (Hyperammonemia)
Organ Transplant Rejection Prophylaxis
Gaucher Disease
Psoriasis Psoriatic Arthritis Ankylosing Spondylitis Non-Radiographic Axial Spondyloarthritis
Cytomegalovirus (CMV) Infections
Chronic Obstructive Pulmonary Disease (COPD)
Iron Overload (Thalassemia, Hemochromatosis)
Hepatitis C
Atopic Dermatitis (Eczema) Asthma with Eosinophilia
Sickle Cell Disease
Crohn's Disease Ulcerative Colitis
Anemia (Chronic Kidney Disease, Cancer Patients)
Idiopathic Pulmonary Fibrosis
Age-related Macular Degeneration Diabetic Macular Edema Retinal Vein Occlusion
Severe Eosinophilic Asthma
Adrenal Insufficiency (Addison's Disease)
Osteoporosis
Short Bowel Syndrome
Type 2 Diabetes
Hemophilia A (with Factor VIII Inhibitors)
Rheumatoid Arthritis Psoriatic Arthritis Ankylosing Spondylitis Crohn's Disease Ulcerative Colitis
Sickle Cell Disease Myeloproliferative Disorders
Iron Deficiency Anemia
Primary Immunodeficiency Disorders Multifocal Motor Neuropathy Guillain-Barré Syndrome
Cystic Fibrosis (Gating Mutations)
Treatment-Resistant Depression Chronic Pain Syndromes
Chronic Gout (Refractory Hyperuricemia)
Age-related Macular Degeneration Diabetic Retinopathy Macular Edema
Pompe Disease
Hypoparathyroidism
Acute Decompensated Heart Failure
Severe Eosinophilic Asthma Eosinophilic Granulomatosis with Polyangiitis (EGPA)
Cystic Fibrosis (F508del Mutation)
Sickle Cell Disease (HbSS and Hbβ0 Thalassemia)
Chronic Hepatitis B Chronic Hepatitis C
Hypercholesterolemia (Familial Hypercholesterolemia)
Pulmonary Arterial Hypertension
Hypercholesterolemia (Familial and Non-Familial)
Pulmonary Arterial Hypertension Erectile Dysfunction
Non-Hodgkin Lymphoma Chronic Lymphocytic Leukemia Rheumatoid Arthritis Granulomatosis with Polyangiitis (GPA) Microscopic Polyangiitis (MPA)
Secondary Hyperparathyroidism Hypercalcemia in Parathyroid Cancer
Paroxysmal Nocturnal Hemoglobinuria (PNH) Atypical Hemolytic Uremic Syndrome (aHUS)
Spinal Muscular Atrophy (SMA)
Psoriasis Psoriatic Arthritis Crohn's Disease Ulcerative Colitis
Hypothyroidism
Thyroid Eye Disease
Cystic Fibrosis (F508del, F508del/Minimal Function, and other Mutations)
Osteoporosis Bone Metastases
Allergic Asthma Chronic Idiopathic Urticaria
Spinal Muscular Atrophy (SMA) - Pediatric Patients